Click chemistry Cerebellum Quality control Inflammation Identity Duchenne Clinical trial AAV Gene-therapy GRMD dog Innate immunity Vector Immunomodulation Immune response Animals Impurities AAV vectors CD8 + T lymphocytes Antibodies/immunology/metabolism Accelerometry Gene therapy AUC Age Humoral immunity Adeno-associated virus Immunogenicity inflammation gene therapy AAV High-throughput technology Homologous recombination Beta-subunit Calcium Capsid Treg Immune responses AAP Inherited retinal dystrophies Fluid-air exchange GC-content Antibody responses Ectopic expression Adenoviridae/immunology Capsid assembly AAV vector Assembly-activating protein B-Lymphocytes/immunology/metabolism DMD Discriminant analysis Baculovirus expression vector Congenital amaurosis Bioconjugates Immunosuppression GRMD Gene transfer Skeletal muscle Analytical ultracentrifugation Mice Dynamin 2 Exon skipping ABCA4 Identity assay High-throughput sequencing Capsid thermostability Exercise Gene Transfer Intra-cerebrospinal fluid injection In vivo Eye surgery Homopolymers Acute treatment Animal model Manufacturing Crigler–Najjar Syndrome Tolerance Cone photoreceptors Bioorthogonality Air tamponade Infectivity Baculovirus CMC Insect cells Immunogenicity Gait assessment Dystrophin Clinical trials Centronuclear myopathy Intravitreal Engineering Cell–virus interaction DMDmdx rat Childhood blindness Dose study CNS Duchenne muscular dystrophy Homogeneity Genes Human-monocyte-derived dendritic cells Gene Therapy Cell therapy Intrathymic gene transfer Capsid thermal stability Adenoassociated viral vector